- 1998 – Hydroxyurea is the first drug approved to treat sickle cell disease in adults for 20+ years
- 2017 – L-glutamine (Endari) approved to treat sickle cell disease in adults and children
- 2017 – Hydroxyurea (Siklos) approved to treat sickle cell disease in children
More Hope on the Horizon
Clinical studies happen in phases, as researchers learn more about the safety and effectiveness of the new drug for humans.
There are clinical studies looking for participants so that they can conduct the research necessary to advance understanding about potential therapies and treatments.
number of phase 01 sickle cell studies curently recruiting
number of phase 02 sickle cell studies curently recruiting
number of phase 03 sickle cell studies curently recruiting
Information per clinicaltrials.gov, 5/4/19. Visit clinicaltrials.gov to learn more about recruitment and participation in clinical trials.
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Take our “Ask Your Doctor” sheet to your physician to start a conversation about clinical studies. There are 5 questions that will help you learn more about studies in your area.
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