Clinical studies are critical to the drug development process
Through clinical studies, teams of medical professionals find new ways to diagnose, treat, and cure diseases. Treatments may include new drugs that are being used in humans for the first time, new surgical procedures, or new ways to use existing treatments. The goal of the study is to determine the safety and effectiveness of the therapy, device, or procedure.
Clinical studies can also simply observe patients — to improve the diagnosis process and the quality of life for people with chronic illnesses. Both healthy people and those with a disease or illness may participate in clinical studies.
Clinical studies offer many potential benefits to people with sickle cell disease, including:
- Access to new treatments before they are widely available
- Regular and careful monitoring of the disease by a team of medical professionals
- Opportunities to learn more about advancements in sickle cell treatments